Achieving Improved Outcomes in Children and Infants with Spinal Muscular Atrophy

Achieving Improved Outcomes in Children and Infants with Spinal Muscular Atrophy

CME/CE Symposium at the 2019 American Academy of Pediatrics National Conference and Exhibition


Monday, October 28th, 2019

6:00 pm – 6:30 pm: Dinner and Registration

6:30pm – 8:00pm CME/CE Program


Hilton New Orleans Riverside
Churchill D
2 Poydras Street
New Orleans, LA 70130
Now Open

Target Audience:

Pediatricians, neurologists, primary care physicians, PAs, NPs, and other healthcare providers involved in the management of patients with SMA

Program Overview:

This CME/CE activity will outline best practices for achieving improved outcomes in children and infants with spinal muscular atrophy (SMA). The faculty will first delve into the pathophysiology, genetics and diagnostics of SMA, as well as disease progression and potential biomarkers. Recent clinical trial data of both emerged and emerging agents will be reviewed as it relates to clinical decision making for healthcare professionals. Following, the faculty will discuss therapeutic strategies utilizing the interprofessional team, with the goal of improving outcomes as quality of life for SMA patients. This interactive, CME/CE symposium will equip the healthcare team with the tools to better treat and manage their patients with spinal muscular atrophy.


  • Welcome, Dinner and Introductions
  • Spinal Muscular Atrophy: Pathophysiology, Genetics, Diagnostics/Screening, Disease Progression and Potential Biomarkers
  • Interactive Panel Discussion
  • Clinical Trial Review of Therapeutics for the Treatment of SMA
  • Interactive Panel Discussion
  • Case Series, Therapeutic Strategies and the Role of the Interprofessional Healthcare Team
  • Interactive Panel Discussion


Claudia A. Chiriboga, MD, MPH (Course Chair)
Professor of Neurology and Pediatrics
Columbia University Medical Center
New York, New York

John F. Brandsema, MD
Assistant Professor of Clinical Neurology
Children’s Hospital of Philadelphia
Philadelphia, Pennsylvania

Stephen L. Nelson, Jr, MD, PhD
Section Head, Pediatric Neurology
Associate Professor of Pediatrics, Neurology, and Psychiatry
Tulane University School of Medicine
New Orleans, Louisiana

Julie A. Parsons, MD
Professor of Clinical Pediatrics and Neurology
Haberfeld Family Endowed Chair in Pediatric Neuromuscular Disorders
Co-Director, Neuromuscular Clinic
Children’s Hospital Colorado
University of Colorado School of Medicine
Aurora, Colorado

Accreditation Statement:

In support of improving patient care, AcademicCME is jointly accredited by the Accreditation Council for Continuing Medical Education (ACCME), the Accreditation Council for Pharmacy Education (ACPE), and the American Nurses Credentialing Center (ANCC), to provide continuing education for the healthcare team.

Credit Designation Statements:

AcademicCME designates this live material for a maximum of 1.50 AMA PRA Category 1 Credits™. Physicians should claim only the credit commensurate with the extent of their participation in the activity.

AcademicCME designates this live material for a maximum of 1.50 CNE contact hours. AcademicCME’s ANCC provider number is P0491.

CE Inquiries/Special Needs:

For all CE inquiries or special needs, please contact [email protected] or 610-687-3300.

Financial Support:

This activity has been supported by an independent educational grant from Biogen


Provided by AcademicCME




* This symposium is neither sponsored nor endorsed by the American Academy of Pediatrics.